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Browsing by Author "E Symington"

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    Efficacy safety and quality of life 4 years after valoctocogene roxaparvovec gene transfer for severe hemophilia A in the phase 3 GENEr81 trial
    A Leavitt; Johnny Mahlangu; P Raheja; E Symington; D Quon; E et al
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    Threeyear outcomes of valoctocogene roxaparvovec gene therapy for hemophilia A
    (WILEY-BLACKWELL) B Madan; M OZELO; P Raheja; E Symington; E et al; Johnny Mahlangu

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