mRNA therapy corrects defective glutathione metabolism and restores ureagenesis in preclinical argininosuccinic acidura

Sonam GurungOskar TimmermandDany PerocheauAna Gil-MartinezE et alSimon Waddington2024-11-192024-11-19WOS1946-6234https://hdl.handle.net/10539/42729mRNA therapy corrects defective glutathione metabolism and restores ureagenesis in preclinical argininosuccinic aciduraJournal Article