Health-related quality of life following valoctocogene roxaparvovec gene therapy for severe hemophilia A in the phase 3 trial GENEr8-1

Brian O' MahonyAmy L DunnAndrew D LeavittF PeyvandiJohnny MahlanguE et al2024-07-232024-07-23WOS1538-7933https://hdl.handle.net/10539/39497Health-related quality of life following valoctocogene roxaparvovec gene therapy for severe hemophilia A in the phase 3 trial GENEr8-1Journal Article