A LeavittJohnny MahlanguP RahejaE SymingtonD QuonE et al2025-03-10WOShttps://hdl.handle.net/10539/44179Efficacy safety and quality of life 4 years after valoctocogene roxaparvovec gene transfer for severe hemophilia A in the phase 3 GENEr81 trialJournal Article